Asciminib Roll-over Study

An Open Label, Multi-center Asciminib Roll-over Study to Assess Long-term Safety in Patients Who Have Completed a Novartis Sponsored Asciminib Study and Are Judged by the Investigator to Benefit From Continued Treatment

ClinicalTrials.gov Identifier: NCT04877522

Novartis Reference Number: CABL001A2001B

Last Update: Jan 30, 2023

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All compounds are either investigational or being studied for (a) new use(s). Efficacy and safety have not been established. There is no guarantee that they will become commercially available for the use(s) under investigation. 

Study Description

This is a long term safety study for patients who have completed a Novartis sponsored asciminib study and are judged by the investigator to benefit from continued treatment

Condition 
Chronic Myelogenous Leukemia
Leukemia, Myelogenous, Chronic, BCR-ABL Positive
Phase 
Phase 3
Overall status 
Recruiting
Start date 
Aug 30, 2022
Completion date 
Aug 30, 2027
Gender 
All
Age(s)
18 Years and older (Adult, Older Adult)

Interventions

Drug
Asciminib single agent
Taken orally, twice daily (BID) or once daily (QD), in fasting state
Drug
Asciminib
Taken orally, once daily, in the morning with low-fat meal or twice daily in fasting state
Drug
Imatinib
Taken orally, once daily, in the morning with low-fat meal
Drug
Nilotinib
Taken orally, twice daily, on an empty stomach
Drug
Bosutinib
Taken orally, once daily, with food
Drug
Dasatinib
Taken orally, once daily in a fasted state, 1 or 2 hours before a meal

Eligibility Criteria

Key Inclusion Criteria:

Participant with PH+ CML or PH+ ALL currently receiving treatment with asciminib (single agent or in combination with imatinib, nilotinib or dasatinib), imatinib, nilotinib or bosutinib alone within a Novartis-sponsored study and, in the opinion of the Investigator, would benefit from continued treatment.
Participant has demonstrated compliance on the parent study protocol and is willing and able to comply with scheduled visits, treatment plans and any other study procedures.

Key Exclusion Criteria:

Participant has been discontinued from parent study treatment.
Participant currently has unresolved toxicities reported as possibly related to study treatment in the parent study.
Participant's ongoing treatment is currently approved and reimbursed at country level.
Pregnant or nursing (lactating) women.
Women of child-bearing potential, unless they are using highly effective methods of contraception and willing to continue while taking study treatment.
Sexually active males receiving imatinib, nilotinib, bosutinib or dasatinib unwilling to follow the relevant contraception requirements in the local prescribing information.

Applicable only for participants on bosutinib treatment that switch to asciminib treatment at enrollment:

Asymptomatic pancreatitis
abnormal ECG
any grade 3 or 4 toxicity not resolved to grade 2 or lower within 28 days before starting asciminib treatment

Other protocol-defined Inclusion/Exclusion criteria may apply.

Study Locations

United States
Michigan Medicine University of Michigan
Recruiting
Ann Arbor, 48109 5271 - Michigan
Contact: Nancy McCullough - [email protected] - Moshe Talpaz
United States
Memorial Sloan Kettering
Recruiting
New York, 10017 - New York
Contact: Dalisa Espinosa (646-497-9068) - [email protected] - Michael Mauro
United States
Oregon Health and Science University
Recruiting
Portland, 97239 - Oregon
Contact: Skyler Foley (+1 503 346 7894) - [email protected] - Michael Charles Heinrich
United States
University of Texas MD Anderson Cancer Center
Recruiting
Houston, 77030 - Texas
Contact: (713-792-2921) Koji Sasaki
United States
Argentina
Novartis Investigative Site
Recruiting
Caba, C1221ADC
Buenos Aires
Argentina
Brazil
Novartis Investigative Site
Recruiting
Rio de Janeiro, 20211-030
RJ
Brazil
Novartis Investigative Site
Recruiting
Sao Paulo, 05403 000
SP
Brazil
Novartis Investigative Site
Recruiting
Sao Paulo, 08270-070
SP
Brazil
Bulgaria
Novartis Investigative Site
Recruiting
Varna, 9000
-
Bulgaria
Canada
Novartis Investigative Site
Recruiting
Montreal, H1T 2M4
Quebec
Canada
Czech Republic
Novartis Investigative Site
Recruiting
Ostrava, 708 52
Poruba
Czech Republic
Novartis Investigative Site
Recruiting
Brno-Bohunice, 639 00
-
Czech Republic
Denmark
Novartis Investigative Site
Recruiting
Copenhagen, DK-2100
-
Denmark
France
Novartis Investigative Site
Recruiting
Bordeaux, 33076
-
France
Novartis Investigative Site
Recruiting
Marseille, 13273
-
France
Novartis Investigative Site
Recruiting
Paris Cedex 10, 75475
-
France
Novartis Investigative Site
Recruiting
Vandoeuvre les Nancy, 54511
-
France
Germany
Novartis Investigative Site
Recruiting
Berlin, 13353
-
Germany
Novartis Investigative Site
Recruiting
Frankfurt, 60590
-
Germany
Novartis Investigative Site
Recruiting
Jena, 07740
-
Germany
Italy
Novartis Investigative Site
Recruiting
Milano, 20162
MI
Italy
Novartis Investigative Site
Recruiting
Roma, 00161
RM
Italy
Novartis Investigative Site
Recruiting
Napoli, 80132
-
Italy
Japan
Novartis Investigative Site
Recruiting
Kobe-shi, 650-0017
Hyogo
Japan
Lebanon
Novartis Investigative Site
Recruiting
Beirut, 1107 2020
-
Lebanon
Mexico
Novartis Investigative Site
Recruiting
Monterrey, 64460
Nuevo Leon
Mexico
Poland
Novartis Investigative Site
Recruiting
Krakow, 31-501
-
Poland
Novartis Investigative Site
Recruiting
Warszawa, 02 776
-
Poland
Novartis Investigative Site
Recruiting
Wroclaw, 50 367
-
Poland
Portugal
Novartis Investigative Site
Recruiting
Lisboa, 1099 023
-
Portugal
Novartis Investigative Site
Recruiting
Porto, 4200-072
-
Portugal
Romania
Novartis Investigative Site
Recruiting
Timisoara, 300079
-
Romania
Russian Federation
Novartis Investigative Site
Recruiting
Moscow, 125167
-
Russian Federation
Novartis Investigative Site
Recruiting
Moscow, 125284
-
Russian Federation
Novartis Investigative Site
Recruiting
Saint Petersburg, 197341
-
Russian Federation
Novartis Investigative Site
Recruiting
St Petersburg, 191024
-
Russian Federation
Spain
Novartis Investigative Site
Recruiting
Sevilla, 41009
Andalucia
Spain
Novartis Investigative Site
Recruiting
Barcelona, 08036
Catalunya
Spain
Novartis Investigative Site
Recruiting
Hospitalet de LLobregat, 08907
Catalunya
Spain
Novartis Investigative Site
Recruiting
Bilbao, 48013
Pais Vasco
Spain
Novartis Investigative Site
Recruiting
Madrid, 28006
-
Spain
Novartis Investigative Site
Recruiting
Madrid, 28034
-
Spain
Novartis Investigative Site
Recruiting
Valencia, 46026
-
Spain
Taiwan
Novartis Investigative Site
Recruiting
Taoyuan, 33305
-
Taiwan
Turkey
Novartis Investigative Site
Recruiting
Samsun, 55139
-
Turkey
United Kingdom
Novartis Investigative Site
Recruiting
Oxford, OX3 7LJ
-
United Kingdom

Contacts

Name: 
Novartis Pharmaceuticals
Phone: 
Name: 
Novartis Pharmaceuticals
Phone: 

Have a question?

Call 1-888-669-6682 or email [email protected]